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Autoimmunity
CMS
Neuromuscular diseases
Treatment
RNA biology
Humans
Lamin A/C LMNA gene
Rare diseases
RNA interference
Inflammation
Cytoskeleton
Calcium
Regeneration
Alternative splicing
Autophagy
Dystrophin
Motoneuron
Animals
Exercise
Heart failure
Therapy
Satellite cell
Satellite cells
Fabry disease
Myotonic Dystrophy type 1
Myopathy
Brain
Becker muscular dystrophy
Errance diagnostique
Glutamate
DMD
Myoblasts
Centronuclear myopathy
OPMD
MBNL
Lamin A/C
Cardiomyopathy
LMNA gene
Muscle regeneration
Nuclear envelope
Rare neuromuscular diseases
Cell therapy
Muscular dystrophy
Biomarker
Neuromuscular junction
Congenital myopathy
Transgenic mouse model
Myotonic dystrophy type 1
Mouse model
Antisense oligonucleotides
Gene therapy
Biomarkers
CRISPRi
Myopathies
AAV
Transcriptomics
Dilated cardiomyopathy
Myotonic dystrophy
Cytokines
Laminopathy
Laminopathies
Autoantibodies
Thérapie génique
Skeletal muscle
Myositis
FSHD
Mechanotransduction
Aged
Cancer
Heart
Aging
Laminopathie
Neuromuscular disease
Congenital muscular dystrophy
Muscle
Long read sequencing
Thymus
Genotype phenotype correlation
PABPN1
Myasthenia Gravis MG
Myogenesis
Diagnosis
Fibrosis
Actin
Autoimmune diseases
Myotonic Dystrophy
LMNA
COVID-19
Astrocyte
Myasthenia gravis
ALS
Male
Dermatomyositis
Outcome measures
CTG repeat contractions
Dynamin 2
Trinucleotide repeat expansion
Clinical trials
Duchenne muscular dystrophy
Amyotrophic lateral sclerosis